Category:Orphan drugs
From HandWiki
Here is a list of articles in the Orphan drugs category of the Chemistry portal.
Lists of all drugs that have received orphan status in the United States and Europe are available from the U.S. Food and Drug Administration and the European Commission, respectively:
Pages in category "Orphan drugs"
The following 200 pages are in this category, out of 451 total.
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- Chemistry:Lanadelumab
- Chemistry:Larotrectinib
- Chemistry:Lecanemab
- Chemistry:Lenacapavir
- Chemistry:Leniolisib
- Chemistry:Lenvatinib
- Chemistry:Letermovir
- Chemistry:Lintuzumab
- Biology:Lisocabtagene maraleucel
- Chemistry:Lithium carbonate
- Chemistry:Lomitapide
- Chemistry:Lonafarnib
- Biology:Lonapegsomatropin
- Chemistry:Loncastuximab tesirine
- Chemistry:Lorlatinib
- Chemistry:Losartan
- Chemistry:Losmapimod
- Biology:Lovotibeglogene autotemcel
- Chemistry:Lumacaftor
- Biology:Lumasiran
- Chemistry:Lurbinectedin
- Biology:Luspatercept
- Chemistry:Lusutrombopag
- Chemistry:Lutetium (177Lu) chloride
- Chemistry:Lutetium (177Lu) oxodotreotide
M
- Chemistry:Maralixibat chloride
- Chemistry:Margetuximab
- Chemistry:Maribavir
- Chemistry:Mavacamten
- Chemistry:Mecasermin rinfabate
- Chemistry:Melatonin as a medication and supplement
- Chemistry:Melphalan
- Chemistry:Melphalan flufenamide
- Chemistry:Mepolizumab
- Chemistry:Metformin
- Chemistry:Methotrexate
- Chemistry:Methoxsalen
- Chemistry:Metreleptin
- Chemistry:Mifamurtide
- Biology:Migalastat
- Chemistry:Miglustat
- Chemistry:Mitapivat
- Biology:Mitomycin C
- Chemistry:Mitotane
- Chemistry:Mobocertinib
- Chemistry:Mogamulizumab
- Chemistry:Momelotinib
- Chemistry:Mosunetuzumab
- Chemistry:Motixafortide
- Chemistry:Moxetumomab pasudotox
- Chemistry:Moxidectin
N
O
- Chemistry:Obeticholic acid
- Chemistry:Obiltoxaximab
- Chemistry:Obinutuzumab
- Chemistry:Octreotide
- Chemistry:Odevixibat
- Chemistry:Olaparib
- Chemistry:Olaratumab
- Chemistry:Olipudase alfa
- Chemistry:Olutasidenib
- Chemistry:Omacetaxine mepesuccinate
- Chemistry:Omaveloxolone
- Chemistry:Omidubicel
- Chemistry:Omigapil
- Biology:Onasemnogene abeparvovec
- Biology:Oncophage
- Biology:ONCOS-102
- Chemistry:Osilodrostat
- Biology:OTL-103
- Chemistry:Oxytocin
P
- Chemistry:Pacritinib
- Chemistry:Pafolacianine
- Chemistry:Palopegteriparatide
- Chemistry:Palovarotene
- Chemistry:Panobinostat
- Chemistry:Paromomycin
- Chemistry:Pasireotide
- Biology:Patisiran
- Chemistry:Pazopanib
- Chemistry:Pegcetacoplan
- Biology:Pegunigalsidase alfa
- Biology:Pegvaliase
- Chemistry:Pegzilarginase
- Chemistry:Pembrolizumab
- Chemistry:Pemigatinib
- Chemistry:Pemtumomab
- Chemistry:Perflubron
- Biology:Pevonedistat
- Chemistry:Pexidartinib
- Organization:Pharmaceutical Accountability Foundation
- Chemistry:Pimozide
- Chemistry:Pirfenidone
- Chemistry:Pirtobrutinib
- Chemistry:Pitolisant
- Chemistry:Plasminogen (medication)
- Chemistry:Plerixafor
- Chemistry:Polatuzumab vedotin
- Chemistry:Pomalidomide
- Chemistry:Posaconazole
- Chemistry:Pozelimab
- Chemistry:Pralsetinib
- Chemistry:Pretomanid
- Chemistry:Protein-bound paclitaxel
- Chemistry:Prothrombin complex concentrate
R
- Chemistry:Ranibizumab
- Chemistry:Ranirestat
- Chemistry:Rasagiline
- Chemistry:Ravulizumab
- Chemistry:Recombinant human parathyroid hormone
- Biology:Remdesivir
- Chemistry:Repotrectinib
- Chemistry:Retifanlimab
- Chemistry:Retigabine
- Chemistry:Retinyl palmitate
- Chemistry:Rexin G
- Chemistry:Rezafungin
- Chemistry:Ribitol
- Chemistry:Rifampicin
- Chemistry:Rifapentine
- Chemistry:Rifaximin
- Chemistry:Rilonacept
- Chemistry:Rimeporide
- Chemistry:Rintatolimod
- Chemistry:Ripretinib
- Chemistry:Risdiplam
- Chemistry:Rituximab
- Chemistry:Romidepsin
- Chemistry:Romiplostim
- Chemistry:Ropeginterferon alfa-2b
- Chemistry:Rovalpituzumab tesirine
- Chemistry:Rozanolixizumab
- Chemistry:Rucaparib
- Chemistry:Ruxolitinib
- Biology:RVT-802
S
- Chemistry:Sacituzumab govitecan
- Chemistry:Sacrosidase
- Chemistry:Sapacitabine
- Chemistry:Satralizumab
- Chemistry:Sebelipase alfa
- Chemistry:Selinexor
- Chemistry:Selpercatinib
- Chemistry:Selumetinib
- Chemistry:Setanaxib
- Chemistry:Setmelanotide
- Chemistry:Silmitasertib
- Chemistry:Sirolimus
- Chemistry:Sobetirome
- Chemistry:Sodium nitrite
- Medicine:Sodium nitrite (medical use)
- Biology:Sodium oxybate
- Biology:Sodium phenylbutyrate
- Chemistry:Sodium stibogluconate
- Chemistry:Sodium thiosulfate
- Chemistry:Solriamfetol
- Biology:Somapacitan
- Chemistry:Somatrogon
- Chemistry:Sorafenib
- Chemistry:Sotalol
- Chemistry:Soticlestat
- Chemistry:Sotorasib
- Chemistry:Sparsentan
- Chemistry:Spesolimab
- Chemistry:Stiripentol
- Biology:Strimvelis
- Chemistry:Sutimlimab
T
- Chemistry:Tabelecleucel
- Chemistry:Tacrolimus
- Chemistry:Tafamidis
- Chemistry:Tafasitamab
- Chemistry:Tafenoquine
- Chemistry:Tagraxofusp
- Chemistry:Talquetamab
- Chemistry:Tamoxifen
- Chemistry:Tazemetostat
- Chemistry:Tebentafusp
- Chemistry:Teclistamab
- Chemistry:Tecovirimat
- Chemistry:Teduglutide
- Chemistry:Temsirolimus
- Chemistry:Tepotinib
- Chemistry:Teprotumumab
- Chemistry:Terguride
- Chemistry:Tetrabenazine
- Biology:Tetrahydrobiopterin
- Chemistry:Tezacaftor
- Chemistry:Tezepelumab
- Chemistry:Thiotepa